The new data show that an axonal injury and neurodegeneration biomarker was reduced in nearly all study participants treated with Spinraza. The evaluates clinical outcomes and safety following ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

Spinal and bulbar muscular atrophy (SBMA), also known as Kennedy’s disease, is a rare genetic disorder. It affects certain nerve cells in the spinal cord and the brainstem. “Bulbar” refers to a ...

Spinal muscular atrophy is a progressive neurodegenerative disease that affects the central nervous system, peripheral nervous system and voluntary muscle movement, according to the Muscular Dystrophy ...

Amyotrophic lateral sclerosis (ALS), known as Lou Gehrig's disease, is an incurable neurological disorder affecting motor neurons—nerve cells in the brain and spinal cord that control voluntary muscle ...

Amyotrophic lateral sclerosis (ALS) is a progressive disease of the nervous system. It affects nerve cells in the brain and spinal cord called motor neurons. Motor neurons control muscle movement and ...

Imagine losing your ability to speak or move, yet still having so much to say. For Brad G. Smith, this became his reality after being diagnosed with ALS, a rare and progressive disease that attacks ...