People with spinal muscle atrophy (SMA), an inherited neuromuscular disease, usually experience muscle weakness that impacts movement. New research suggests that electrical spinal cord stimulation ...
British singer Jesy Nelson recently took to Instagram to share a devastating update about her 8-month-old twin daughters.
The mother of a four-year-old boy with a rare muscle disease says screening newborn babies for the condition could "save ...
Former Little Mix star Jesy Nelson revealed on social media that her twin girls have been diagnosed with a rare genetic ...
The singer shared an emotional update about her twins’ health on Sunday and that ‘time is of the essence with this disease’ ...
The BBC's Ben Morris describes living with spinal muscular atrophy, as former Little Mix star Jesy Nelson reveals her twins ...
This image from video provided by UPMC and University of Pittsburgh Health Sciences shows Doug McCullough, who has spinal muscular atrophy, during tests of experimental spinal cord stimulation to ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
Editor’s note: This is an automatically generated transcript. Please notify editor@healio.com if there are concerns regarding accuracy of the transcription. So most recently, there has been the ...
The least-squares mean difference in the Hammersmith Functional Motor Scale-Expanded change from baseline at 12 months was 1.8 points for those 2 to 12 years receiving apitegromab vs placebo.
Evrysdi, also known as risdiplam, is an oral medicine used to treat spinal muscular atrophy (SMA) in children and adults. SMA is a genetic disease that is passed down through families. It leads to ...