Researchers at Kumamoto University have demonstrated that iron supplementation can significantly alleviate muscle pathology ...

Zeleciment basivarsen (z-basivarsen) demonstrated sustained functional improvement across multiple clinical measures in the ongoing ACHIEVE clinical trial - - Expect to complete enrollment in ACHIEVE ...

Researchers from Carnegie Mellon University have discovered a way to target RNA that could lead to new treatment options for ...

Tributes flooded the internet for Gilbert Gottfried after his family shared on Tuesday via Twitter that he died following “a long illness.” Since then, there has been more awareness around muscular ...

"High clinical suspicion is important for this population of patients. Since muscular dystrophy is progressive in nature, monitoring disease progression in these patients is critical for timing ...

In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...

A Sarepta Therapeutics gene therapy that failed its confirmatory test has now converted its accelerated FDA approval into a traditional one, expanding use of the treatment to a wider group of Duchenne ...

Duchenne Muscular Dystrophy (DMD) is a debilitating genetic disorder that eventually leaves patients in a wheelchair. In a new study, researchers have found that an existing cancer drug shows promise ...

The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...

While it’s established that Duchenne muscular dystrophy (DMD) causes a loss of muscle mass and strength, few studies have examined the gastrointestinal issues tied to DMD. Initial fractures are the ...

Nila Morton, a graduate student at Howard University, was excited to be traveling back to South Carolina for Thanksgiving after almost a year of being away from home. Morton, 25, was born with a rare ...

Mary Wickizer, center, shows her son Isaac, 7, the keys to their new wheelchair-accessible van while her husband Matt Wickizer looks on during a special presentation on Nov. 22 at Superior Van & ...